Outcomes relevant to treatment decision-making are inconsistently reported in trials involving glomerular disease. Here, we sought to establish a consensus-derived set of critically important outcomes designed to be reported in all future trials by using an online, international two-round Delphi survey in English. To develop this, patients with glomerular disease, caregivers and health professionals aged 18 years and older rated the importance of outcomes using a Likert scale and a Best-Worst scale. The absolute and relative importance was assessed and comments were analyzed thematically. Of 1198 participants who completed Round 1, 734 were patients/caregivers while 464 were healthcare professionals from 59 countries. Of 700 participants that completed Round 2, 412 were patients/caregivers and 288 were healthcare professionals. Need for dialysis or transplant, kidney function, death, cardiovascular disease, remission-relapse and life participation were the most important outcomes to patients/caregivers and health professionals. Patients/caregivers rated patient-reported outcomes higher while healthcare professionals rated hospitalization, death and remission/relapse higher. Four themes explained the reasons for their priorities: confronting death and compounded suffering, focusing on specific targets in glomerular disease, preserving meaning in life, and fostering self-management. Thus, consistent reporting of these critically important outcomes in all trials involving glomerular disease is hoped to improve patient-centered decision-making.Copyright © 2021. Published by Elsevier Inc.
About The Expert
Simon A Carter
Charlotte Logeman
Martin Howell
Dan Cattran
Liz Lightstone
Arvind Bagga
Sean J Barbour
Jonathan Barratt
John Boletis
Dawn J Caster
Rosanna Coppo
Fernando C Fervenza
Jürgen Floege
Michelle A Hladunewich
Jonathan J Hogan
A Richard Kitching
Richard A Lafayette
Ana Malvar
Jai Radhakrishnan
Brad H Rovin
Nicole Scholes-Robertson
Hérnan Trimarchi
Hong Zhang
Yeoungjee Cho
Louese Dunn
Debbie S Gipson
Adrian Liew
Benedicte Sautenet
Andrea K Viecelli
David Harris
David W Johnson
Angela Yee-Moon Wang
Armando Teixeira-Pinto
Stephen I Alexander
Adam Martin GradCert
Allison Tong
Jonathan C Craig
References
PubMed